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Meckel syndrome, type 4

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Clinical Trials

This information is provided by ClinicalTrials.gov

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Displaying 1-2 of 2 results.
Single Ascending Dose Study in Participants With LCA10
Status: Recruiting
Last Changed: Jun 17, 2020
First Received: Mar 13, 2019
Disease(s): Blindness, Leber Congenital Amaurosis 10, Vision Disorders, Eye Diseases, Eye Diseases, Hereditary, Eye Disorders Congenital, Retinal Disease, Retinal Degeneration
Intervention(s): AGN-151587
Locations: Bascom Palmer Eye Institute, Miami, Florida, United States
Massachusetts Eye and Ear Infirmary, Boston, Massachusetts, United States
W.K. Kellogg Eye Center - University of Michigan, Ann Arbor, Michigan, United States
Casey Eye Institute - OSHU, Portland, Oregon, United States
A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)
Status: Recruiting
Last Changed: Jun 25, 2020
First Received: Apr 12, 2019
Disease(s): Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis, Vision Disorders, Sensation Disorders, Neurologic Manifestations, Eye Diseases, Eye Diseases, Hereditary, Eye Disorders Congenital, Retinal Disease
Intervention(s): sepofarsen, Sham
Locations: University of Miami - Bascom Palmer Eye Institute, Miami, Florida, United States
University of Iowa, Iowa City, Iowa, United States
Columbia University Medical Center, New York, New York, United States
Casey Eye Institute - Oregon Health & Science University, Portland, Oregon, United States
University of Pennsylvania - Center for Advanced Retinal & Ocular Therapeutics, Philadelphia, Pennsylvania, United States
... and 13 other locations.